Clinical Protocol: Phase I Clinical Trial Utilizing Gene Therapy for Limb Girdle Muscular Dystrophy: alpha-, beta-, gamma-, or delta-Sarcoglycan Gene Delivered with Intramuscular Instillations of Adeno-Associated Vectors
- 20 March 2000
- journal article
- research article
- Published by Mary Ann Liebert Inc in Human Gene Therapy
- Vol. 11 (5), 777-790
- https://doi.org/10.1089/10430340050015671