Safe and efficient transduction of the liver after peripheral vein infusion of self-complementary AAV vector results in stable therapeutic expression of human FIX in nonhuman primates
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Open Access
- 7 November 2006
- journal article
- Published by American Society of Hematology in Blood
- Vol. 109 (4), 1414-1421
- https://doi.org/10.1182/blood-2006-03-010181
Abstract
The safety and efficacy of peripheral venous administration of a self-complementary adeno-associated viral vector encoding the human FIX gene (scAAV-LKeywords
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