Repair of a Splicing Defect in Erythroid Cells from Patients with β-Thalassemia/HbE Disorder
Open Access
- 31 December 2002
- journal article
- Published by Elsevier in Molecular Therapy
- Vol. 6 (6), 718-726
- https://doi.org/10.1006/mthe.2002.0805
Abstract
No abstract availableKeywords
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