A roundabout route to gene therapy
- 1 April 2002
- journal article
- Published by Springer Nature in Nature Genetics
- Vol. 30 (4), 345-346
- https://doi.org/10.1038/ng0402-345
Abstract
No abstract availableKeywords
This publication has 8 references indexed in Scilit:
- Rescue of a deficiency in ATP synthesis by transfer of MTATP6, a mitochondrial DNA-encoded gene, to the nucleusNature Genetics, 2002
- Manipulating mitochondrial DNA heteroplasmy by a mitochondrially targeted restriction endonucleaseHuman Molecular Genetics, 2001
- Targeting peptide nucleic acid (PNA) oligomers to mitochondria within cells by conjugation to lipophilic cations: implications for mitochondrial DNA replication, expression and diseaseNucleic Acids Research, 2001
- Suppression of Mutations in Mitochondrial DNA by tRNAs Imported from the CytoplasmScience, 2000
- Reversal of a mitochondrial DNA defect in human skeletal muscleNature Genetics, 1997
- Selective inhibition of mutant human mitochondrial DNA replication in vitro by peptide nucleic acidsNature Genetics, 1997
- A novel heteroplasmic tRNAleu(CUN) mtDNA point mutation in a sporadic patient with mitochondrial encephalomyopathy segregates rapidly in skeletal muscle and suggests an approach to therapyHuman Molecular Genetics, 1996
- Assembly of functional proton-translocating ATPase complex in yeast mitochondria with cytoplasmically synthesized subunit 8, a polypeptide normally encoded within the organelle.Proceedings of the National Academy of Sciences, 1988