Minicircle DNA-based Gene Therapy Coupled With Immune Modulation Permits Long-term Expression of α-L-Iduronidase in Mice With Mucopolysaccharidosis Type I
Open Access
- 1 March 2011
- journal article
- Published by Elsevier in Molecular Therapy
- Vol. 19 (3), 450-460
- https://doi.org/10.1038/mt.2010.249
Abstract
No abstract availableKeywords
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